Topic - Sarepta Therapeutics

) is a medical research and drug development company with corporate offices and research facilities in Cambridge, Massachusetts, United States. Incorporated in 1980 as AntiVirals, As of 2018, the company has one approved drug (see the Products section below). - Source: Wikipedia

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FILE - A sign for the Food and Drug Administration is displayed outside their offices in Silver Spring, Md., on Dec. 10, 2020. The first gene therapy for Duchenne muscular dystrophy received preliminary U.S. approval on Thursday, June 22, 2023, despite concerns from some government scientists about the treatment's ability to help boys with the inherited disease. (AP Photo/Manuel Balce Ceneta, File)

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young kids

By Matthew Perrone - Associated Press

This image provided by Sarepta Therapeutics in December 2019 shows a box and vial of their drug Vyondys 53. On Thursday, Dec. 12, 2019, U.S. health regulators said they approved this second drug for a debilitating form of muscular dystrophy, a surprise decision after the medication was rejected for safety concerns just four months earlier. (Sarepta Therapeutics via AP)

In surprise decision, U.S. approves muscular dystrophy drug

By Matthew Perrone - Associated Press