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Topic - Crispr Therapeutics

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Gautam Dongre, of the National Alliance of Sickle Cell Organizations, sits for a portrait with his daughter, Sumedha, 13, at their residence in Nagpur, India, Wednesday, Dec. 6, 2023. Dongre recalls how his newborn son, Girish, cried constantly from stomach and leg pain. Doctors couldn’t figure out what was wrong and didn’t diagnose him with sickle cell for 2 1/2 years. When Sumedha was born, he and his wife had her tested immediately and learned she had the disease too. (AP Photo/Ajit Solanki)

Promising new gene therapies for sickle cell are out of reach in countries where they’re needed most

By Laura Ungar - Associated Press

This microscope photo provided on Oct. 25, 2023, by the Centers for Disease Control and Prevention shows crescent-shaped red blood cells from a sickle cell disease patient in 1972. Britain's medicines regulator has authorized the world's first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in the U.K. In a statement on Thursday, Nov. 16, 2023, the Medicines and Healthcare Regulatory Agency said it approved Casgevy, the first medicine licensed using the gene editing tool CRISPR, which won its makers a Nobel prize in 2020. (Dr. F. Gilbert/CDC via AP, File )

The world’s first gene therapy for sickle cell and thalassemia has been approved

By Maria Cheng - Associated Press

FILE - This July 2019 image provided by the Sarah Cannon Research Institute shows Victoria Gray on her infusion day during a gene editing trial for sickle cell disease at the Sarah Cannon Research Institute and The Children's Hospital At TriStar Centennial in Nashville. Gray, the first patient to test the treatment, shared her experience with researchers at a scientific conference in 2023. She described suffering with terrible bouts of pain since childhood and receiving high-dose pain medications and sometimes blood transfusions. She described feeling she "was being reborn” the day she got the gene therapy. (Anthem Pictures/Sarah Cannon Research Institute via AP, File)

A new cure for sickle cell disease may be coming. Health advisers will review it next week

By Laura Ungar - Associated Press

This July 2019 image provided by the Sarah Cannon Research Institute shows Victoria Gray on her infusion day during a gene editing trial for sickle cell disease at the Sarah Cannon Research Institute and The Children's Hospital At TriStar Centennial in Nashville. Since her treatment, Gray has weaned herself from pain medications she depended on to manage her symptoms. (Anthem Pictures/Sarah Cannon Research Institute via AP)

Gene-editing treatment shows promise for sickle cell disease

By MARION RENAULT - Associated Press